Cure SMA has awarded a $50,000 research grant to Rashmi Kothary, PhD, at the University of Ottawa, for his project, ” The shifting landscape of SMA research: towards a better…
Cure SMA has awarded a $150,000 research grant to Robin Parks, PhD, at the University of Ottawa, for his project, “Serum-derived exosomes as a biomarker for Spinal Muscular Atrophy.” Dr.…
Dear Cure SMA Canada Community, Cure SMA Canada has been working feverishly in our fight for broad access to treatment. A short but important update in these meetings and…
Drug researcher disputes rare disease medication pricing.
If it were not for bad news, the spinal muscular atrophy (SMA) community in Canada would have no news at all. At least in the past couple of…
Cure SMA Canada urges timely, committed negotiations to provide coverage of first-ever and life-saving treatment for debilitating childhood disease. Cure SMA Canada, on behalf of Canadians diagnosed with Spinal Muscular…
Clinical Trials Clinical trials test drug candidates for safety and effectiveness. Clinical Trial Basics A clinical trial, also called an interventional study, tests new drugs and treatments. It can…
The Cure SMA drug pipeline is one of the primary ways we evaluate the success of our research program. The pipeline identifies the major drug programs in development, and tracks…
BIOGEN RESPONDS TO COVERAGE RECOMMENDATION BY THE CANADIAN DRUG EXPERT COMMITTEE (CDEC) FOR SPINRAZA, THE ONLY TREATMENT APPROVED FOR TREATMENT OF 5Q SPINAL MUSCULAR ATROPHY (SMA) Ottawa – December 22,…